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Old 11-02-2019, 07:08 PM
  #20  
mmccombs
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Join Date: Aug 2010
Location: St. Louis, MO
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The $800k is per eye...

It is a gene therapy medication which arrests the progression of a congenital condition ending in blindness. One of the reasons for extremely high price is so few people are impacted. Similar technology has resulted in a treatment for spinal muscular atrophy. In severe cases SMA kills children before the age of 10. This treatment is over $2m. Once again, very small patient pool. Very exciting technology, but until they come up with a treatment for something impacting a larger patient population the unit costs are going to be startling.